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Mirum Pharmaceuticals
Mirum Pharmaceuticals
(MIRM)
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Clinical Trials
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Revenue by Drug
Marketed Drugs
Therapeutic Areas:
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Classification:
All
Include Generics:
Trade Name
Drug Name
Approved
Patent Expires
Indication
Livmarli
Maralixibat
2021-09-29
2031-2040
Pruritus
,
Alagille syndrome
Cholbam
Cholic acid
2015-03-17
Zellweger syndrome
,
Inborn errors metabolism
Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Cholic acid
healthy volunteers/patients
,
type 2 diabetes mellitus
,
lymphoma
,
central nervous system neoplasms
,
hepatic insufficiency
,
alcoholic hepatitis
,
cardiovascular diseases
,
heart diseases
,
syndrome
,
lipodystrophy
,
cleft palate
,
hypospadias
,
x-linked genetic diseases
,
smith-lemli-opitz syndrome
,
hypertelorism
,
hiv
,
metabolic syndrome
,
alcoholic fatty liver
,
head and neck neoplasms
,
end stage liver disease
,
liver diseases
,
fatty liver
,
non-alcoholic fatty liver disease
,
peroxisomal disorders
,
zellweger syndrome
,
infantile refsum disease
,
adrenoleukodystrophy
,
refsum disease
,
inborn errors metabolism
,
inborn errors lipid metabolism
,
inborn errors steroid metabolism
,
cholestasis
,
psoriasis
,
dermatitis
,
hepatitis c
,
chronic hepatitis c
,
hepatitis
,
appetite regulation
,
metabolism
,
aging
,
malnutrition
,
fontan procedure
,
liver cirrhosis
,
fibrosis
,
diabetes mellitus
Maralixibat
overweight
,
healthy volunteers/patients
,
substance withdrawal syndrome
,
biliary atresia
,
cholestasis
,
syndrome
,
alagille syndrome
,
liver diseases
,
intrahepatic cholestasis
,
pruritus
,
fibrosis
,
cystic fibrosis
,
constipation
Maralixibat chloride
overweight
,
healthy volunteers/patients
,
liver cirrhosis
,
biliary liver cirrhosis
,
substance withdrawal syndrome
,
biliary atresia
,
sclerosing cholangitis
,
cholangitis
,
syndrome
,
alagille syndrome
,
liver diseases
,
cholestasis
,
intrahepatic cholestasis
,
fibrosis
,
pruritus
,
cystic fibrosis
,
constipation
Benzocaine
large b-cell lymphoma diffuse
,
multiple myeloma
,
b-cell chronic lymphocytic leukemia
,
follicular lymphoma
,
recurrence
,
lymphoma
,
glioma
,
hodgkin disease
,
mantle-cell lymphoma
,
b-cell lymphoma
,
triple negative breast neoplasms
,
renal cell carcinoma
,
carcinoma
,
hypertension
,
infections
,
chronic hepatitis b
,
communicable diseases
,
lung neoplasms
,
parkinson disease
,
parkinsonian disorders
,
movement disorders
,
dyskinesias
,
myositis
,
giant cell arteritis
,
polymyalgia rheumatica
,
chronic renal insufficiency
,
uveitis
,
pituitary acth hypersecretion
,
acth-secreting pituitary adenoma
,
graft vs host disease
,
type 1 diabetes mellitus
,
hypoglycemia
,
prostatic neoplasms
,
castration-resistant prostatic neoplasms
,
brain neoplasms
,
astrocytoma
,
oligodendroglioma
,
pancreatic neoplasms
,
insulinoma
,
neuroendocrine tumors
,
islet cell carcinoma
,
gastrinoma
,
glucagonoma
,
somatostatinoma
,
mucositis
,
psoriasis
,
breast neoplasms
,
myelodysplastic syndromes
,
thrombocytopenia
,
preleukemia
,
syndrome
,
macular edema
,
retinal vein occlusion
,
vision disorders
,
low vision
,
macular degeneration
,
thrombocytopenic purpura idiopathic
,
thrombocytopenic purpura
,
purpura
,
juvenile arthritis
,
arthritis
,
kidney diseases
,
myocardial infarction
,
infarction
,
inferior wall myocardial infarction
,
organ transplantation
,
wet macular degeneration
,
neoplasm metastasis
,
graft rejection
,
chronic obstructive pulmonary disease
,
lung diseases
,
obstructive lung diseases
,
liver diseases
,
non-alcoholic fatty liver disease
,
fatty liver
,
postoperative pain
,
toothache
,
choroidal neovascularization
,
pathologic neovascularization
,
chronic kidney failure
,
renal insufficiency
,
liver transplantation
,
kidney transplantation
,
hepatitis c
,
hepatitis
,
hepatitis a
,
ankylosing spondylitis
,
spondylarthritis
,
spondylitis
,
liver cirrhosis
,
fibrosis
,
atrial fibrillation
VOLIXIBAT
overweight
,
healthy volunteers/patients
,
non-alcoholic fatty liver disease
,
fatty liver
,
alcoholic fatty liver
,
cholangitis
,
pregnancy complications
,
cholestasis
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
Sodium chloride
septic shock
,
shock
,
osteoarthritis
,
knee osteoarthritis
,
aortic valve stenosis
,
pathologic constriction
,
von willebrand diseases
,
eye diseases
,
joint diseases
,
tibial meniscus injuries
Aspartame
healthy volunteers/patients
,
laron syndrome
,
pituitary dwarfism
,
leukemia
,
myelodysplastic syndromes
,
myeloid leukemia acute
,
megakaryoblastic leukemia acute
,
monocytic leukemia acute
,
myelomonocytic leukemia acute
,
myeloid leukemia
,
erythroblastic leukemia acute
,
neoplasms
,
dyspnea
,
asthma
,
chronic obstructive pulmonary disease
,
lung diseases
,
obstructive lung diseases
,
inflammation
SHP626
overweight
,
healthy volunteers/patients
,
non-alcoholic fatty liver disease
,
fatty liver
,
alcoholic fatty liver
,
cholangitis
,
pregnancy complications
,
cholestasis
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
Arm1
glaucoma
,
pharmacokinetics
,
acute pain
,
asthma
,
ocular hypertension
,
open-angle glaucoma
,
multiple myeloma
,
plasma cell neoplasms
,
healthy volunteers/patients
,
erectile dysfunction
,
death
,
neoplasm metastasis
,
hiv-2
,
neoplasms
,
breast neoplasms
,
prostatic neoplasms
,
lymphoma
,
pancreatic neoplasms
,
castration-resistant prostatic neoplasms
,
triple negative breast neoplasms
,
hypogonadism
,
sarcoma
,
colorectal neoplasms
,
stomach neoplasms
,
glioblastoma
,
biliary tract neoplasms
,
hypertension
,
b-cell lymphoma
,
endometrial neoplasms
,
hepatocellular carcinoma
,
esophageal neoplasms
,
liver neoplasms
,
small cell lung carcinoma
,
disease progression
,
chronic hepatitis
,
liver diseases
,
gastrointestinal diseases
,
virus diseases
,
rna virus infections
,
digestive system diseases
,
viral hepatitis human
,
flaviviridae infections
,
general anesthesia
,
chronic obstructive pulmonary disease
,
lung diseases
,
obstructive lung diseases
,
obstructive sleep apnea
,
sleep apnea syndromes
,
apnea
,
syndrome
,
disorders of excessive somnolence
,
sleepiness
,
papillomavirus infections
,
uterine cervical neoplasms
,
vaginal neoplasms
,
vulvar neoplasms
,
condylomata acuminata
,
hodgkin disease
,
migraine disorders
,
atherosclerosis
,
pancreatic ductal carcinoma
,
uterine neoplasms
,
carcinosarcoma
,
mullerian mixed tumor
,
adenocarcinoma
,
esophageal squamous cell carcinoma
,
large b-cell lymphoma diffuse
,
neuroendocrine tumors
,
intestinal neoplasms
,
head and neck neoplasms
,
prostatic hyperplasia
,
sarcopenia
,
muscular atrophy
,
eunuchism
,
hypertrophy
,
urologic neoplasms
,
transitional cell carcinoma
,
urinary bladder neoplasms
,
microsatellite instability
,
non-small-cell lung carcinoma
,
chronic hepatitis c
,
lung neoplasms
,
type 2 diabetes mellitus
,
diabetes mellitus
,
carcinoma
,
obesity
,
squamous cell carcinoma of head and neck
,
squamous cell carcinoma
,
vomiting
,
nausea
,
melanoma
,
urinary tract infections
,
anesthesia
,
keratoconjunctivitis sicca
,
dry eye syndromes
,
eye diseases
,
overweight
,
polycystic kidney diseases
,
inflammation
,
spondylarthritis
,
spondylitis
,
axial spondyloarthritis
,
neuralgia
,
postherpetic neuralgia
,
hepatitis
,
hepatitis a
,
hepatitis c
,
hiv infections
,
infections
,
communicable diseases
,
hiv
,
acquired immunodeficiency syndrome
,
ovarian neoplasms
,
herpes zoster
,
mumps
,
measles
,
chickenpox
,
rubella
,
kidney diseases
,
rheumatoid arthritis
,
arthritis
,
ovarian epithelial carcinoma
,
hepatitis a virus
,
immunosuppression therapy
,
hemorrhage
,
chronic renal insufficiency
,
chronic disease
,
drug-related side effects and adverse reactions
,
non-hodgkin lymphoma
,
follicular lymphoma
Arm2
glaucoma
,
pharmacokinetics
,
multiple myeloma
,
plasma cell neoplasms
,
acute pain
,
asthma
,
erectile dysfunction
,
ocular hypertension
,
open-angle glaucoma
,
healthy volunteers/patients
,
death
,
neoplasm metastasis
,
neoplasms
,
prostatic neoplasms
,
breast neoplasms
,
pancreatic neoplasms
,
lymphoma
,
hypogonadism
,
sarcoma
,
castration-resistant prostatic neoplasms
,
glioblastoma
,
chronic hepatitis
,
colorectal neoplasms
,
ovarian neoplasms
,
triple negative breast neoplasms
,
biliary tract neoplasms
,
adenocarcinoma
,
hepatocellular carcinoma
,
liver neoplasms
,
hypertension
,
small cell lung carcinoma
,
disease progression
,
stomach neoplasms
,
malignant mesothelioma
,
mesothelioma
,
urinary bladder neoplasms
,
microsatellite instability
,
head and neck neoplasms
,
urologic neoplasms
,
transitional cell carcinoma
,
liver diseases
,
gastrointestinal diseases
,
virus diseases
,
rna virus infections
,
digestive system diseases
,
viral hepatitis human
,
flaviviridae infections
,
chronic obstructive pulmonary disease
,
lung diseases
,
obstructive lung diseases
,
obstructive sleep apnea
,
sleep apnea syndromes
,
apnea
,
syndrome
,
disorders of excessive somnolence
,
sleepiness
,
prostatic hyperplasia
,
sarcopenia
,
muscular atrophy
,
eunuchism
,
hypertrophy
,
papillomavirus infections
,
uterine cervical neoplasms
,
vaginal neoplasms
,
vulvar neoplasms
,
condylomata acuminata
,
esophageal squamous cell carcinoma
,
migraine disorders
,
large b-cell lymphoma diffuse
,
b-cell lymphoma
,
pancreatic ductal carcinoma
,
endometrial neoplasms
,
esophageal neoplasms
,
uterine neoplasms
,
carcinosarcoma
,
mullerian mixed tumor
,
non-small-cell lung carcinoma
,
lung neoplasms
,
type 2 diabetes mellitus
,
diabetes mellitus
,
chronic hepatitis c
,
carcinoma
,
vomiting
,
melanoma
,
squamous cell carcinoma of head and neck
,
squamous cell carcinoma
,
obesity
,
nausea
,
polycystic kidney diseases
,
anesthesia
,
fever
,
diarrhea
,
keratoconjunctivitis sicca
,
dry eye syndromes
,
eye diseases
,
overweight
,
neuralgia
,
postherpetic neuralgia
,
hepatitis
,
hepatitis a
,
hepatitis c
,
infections
,
communicable diseases
,
hiv infections
,
hiv
,
kidney diseases
,
acquired immunodeficiency syndrome
,
herpes zoster
,
mumps
,
measles
,
chickenpox
,
rubella
,
chronic renal insufficiency
,
chronic disease
,
hemorrhage
,
hepatitis a virus
,
drug-related side effects and adverse reactions
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