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Mirum Pharmaceuticals
Mirum Pharmaceuticals
(MIRM)
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Clinical Trials
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Revenue by Drug
Marketed Drugs
Therapeutic Areas:
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Classification:
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Include Generics:
Trade Name
Drug Name
Approved
Patent Expires
Indication
Livmarli
Maralixibat
2021-09-29
2031-2040
Pruritus
,
Alagille syndrome
Cholbam
Cholic acid
2015-03-17
Zellweger syndrome
,
Inborn errors metabolism
Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Cholic acid
neurofibromatosis 1
,
neurofibroma
,
hyperlipidemias
,
central nervous system neoplasms
,
neurofibromatoses
,
aging
,
clostridium infections
,
colonic neoplasms
,
rectal neoplasms
,
echolocation
,
hyperlipoproteinemia type iv
,
metabolic syndrome
,
hypertriglyceridemia
,
familial combined hyperlipidemia
,
liver function tests
,
gastric bypass
,
alcoholic hepatitis
,
parkinson disease
,
huntington disease
,
cardiovascular diseases
,
heart diseases
,
hepatitis a
,
alcoholic fatty liver
,
lipoma
,
gastrointestinal diseases
,
digestive system diseases
,
liver neoplasms
,
lipodystrophy
,
rheumatoid arthritis
,
arthritis
,
biliary tract diseases
,
barrett esophagus
,
reperfusion injury
,
heart failure
,
cystic fibrosis
,
covid-19
,
muscle spasticity
,
hereditary spastic paraplegia
,
paraplegia
,
irritable bowel syndrome
,
constipation
,
cardiomyopathies
,
disease progression
,
amyloidosis
,
neoplasm metastasis
,
radiation injuries
,
body weight
,
insulin resistance
,
amyotrophic lateral sclerosis
,
motor neuron disease
,
sclerosis
,
cleft palate
,
hypospadias
,
x-linked genetic diseases
,
smith-lemli-opitz syndrome
,
hypertelorism
,
hiv
,
pruritus
,
bile duct diseases
,
adolescent development
,
sarcoidosis
,
polycystic kidney diseases
,
autosomal dominant polycystic kidney
,
cysts
,
obstructive jaundice
,
jaundice
,
esophageal neoplasms
,
head and neck neoplasms
,
end stage liver disease
,
hepatitis d
,
coinfection
,
breast neoplasms
,
acute kidney injury
,
kidney neoplasms
,
cholestasis
,
healthy volunteers/patients
,
intrahepatic cholestasis
,
colorectal neoplasms
,
cerebrotendinous xanthomatosis
,
xanthomatosis
,
malnutrition
,
neoplasms
,
pregnancy complications
,
glucose intolerance
,
sclerosing cholangitis
,
peroxisomal disorders
,
zellweger syndrome
,
infantile refsum disease
,
adrenoleukodystrophy
,
refsum disease
,
adenomatous polyposis coli
,
nasopharyngeal neoplasms
,
adenoma
,
retinal detachment
,
dissociative disorders
,
chronic hepatitis c
,
duodenal neoplasms
,
inborn errors metabolism
,
inborn errors lipid metabolism
,
inborn errors steroid metabolism
,
pregnancy
,
follicular lymphoma
,
inborn genetic diseases
,
sepsis
,
child nutrition disorders
,
ulcerative colitis
,
pouchitis
,
thyroid diseases
,
acute cholecystitis
,
cholecystitis
,
acalculous cholecystitis
,
pancreatitis
,
psoriasis
,
biliary liver cirrhosis
,
liver diseases
,
fibrosis
,
liver cirrhosis
,
non-alcoholic fatty liver disease
,
cholangitis
,
fatty liver
,
type 2 diabetes mellitus
,
diabetes mellitus
,
gallstones
,
cholelithiasis
,
cholecystolithiasis
,
obesity
,
morbid obesity
,
syndrome
,
hepatitis
,
chemical and drug induced liver injury
,
dyspepsia
,
gestational diabetes
,
overweight
,
autoimmune hepatitis
,
fatigue
,
adiposity
,
neonatal hyperbilirubinemia
,
malabsorption syndromes
,
lipid metabolism disorders
,
diarrhea
,
hemolysis
,
hemolytic anemia
,
chronic kidney failure
,
kidney diseases
,
short bowel syndrome
,
cardiac surgical procedures
,
precursor cell lymphoblastic leukemia-lymphoma
,
lymphoid leukemia
,
fontan procedure
,
infections
,
communicable diseases
,
dermatitis
,
brain neoplasms
,
sarcoma
,
germ cell and embryonal neoplasms
,
medulloblastoma
,
retinoblastoma
,
rhabdoid tumor
,
ewing sarcoma
,
rhabdomyosarcoma
,
primitive neuroectodermal tumors
,
hepatoblastoma
,
retinal neoplasms
,
neuroectodermal tumors
,
phenylketonurias
,
appetite regulation
,
ischemia
,
liver transplantation
,
gastroesophageal reflux
,
metabolism
,
biliary atresia
,
liver regeneration
,
hepatocellular carcinoma
,
cholangiocarcinoma
,
liver failure
,
hyperbilirubinemia
,
hepatomegaly
,
glucosephosphate dehydrogenase deficiency
,
hepatic encephalopathy
,
transjugular intrahepatic portasystemic shunt
,
hepatitis b
,
hepatitis e
Chenodiol
cerebrotendinous xanthomatosis
,
xanthomatosis
Maralixibat
overweight
,
healthy volunteers/patients
,
syndrome
,
biliary liver cirrhosis
,
substance withdrawal syndrome
,
biliary tract diseases
,
bile duct diseases
,
biliary atresia
,
digestive system diseases
,
sclerosing cholangitis
,
alagille syndrome
,
liver diseases
,
intrahepatic cholestasis
,
cholestasis
,
pruritus
Maralixibat chloride
overweight
,
healthy volunteers/patients
,
syndrome
,
biliary liver cirrhosis
,
biliary tract diseases
,
bile duct diseases
,
substance withdrawal syndrome
,
digestive system diseases
,
biliary atresia
,
sclerosing cholangitis
,
cystic fibrosis
,
constipation
,
alagille syndrome
,
intrahepatic cholestasis
,
liver diseases
,
cholestasis
,
pruritus
Benzocaine
osteoarthritis
,
neoplasms
,
chronic obstructive pulmonary disease
,
arthritis
,
lung diseases
,
obstructive lung diseases
,
psoriatic arthritis
,
allergic rhinitis
,
rhinitis
,
respiratory tract diseases
,
asthma
,
bronchial diseases
,
hemangioma
,
kaposi sarcoma
,
kasabach-merritt syndrome
,
hemangioendothelioma
,
down syndrome
,
syndrome
,
cognitive dysfunction
,
hiv-1
,
pruritus
,
chronic urticaria
,
urticaria
,
breast neoplasms
,
dwarfism
,
crohn disease
,
alopecia areata
,
alopecia
,
candidemia
,
invasive candidiasis
,
renal insufficiency
,
carotid artery diseases
,
atherosclerosis
,
neoplasm metastasis
,
endocrine system diseases
,
laron syndrome
,
pituitary dwarfism
,
juvenile arthritis
,
chronic disease
,
failure to thrive
,
psychotic disorders
,
mood disorders
,
mental disorders
,
hair diseases
,
tobacco use disorder
,
anxiety disorders
,
emphysema
,
pulmonary emphysema
,
ulcerative colitis
,
colitis
,
ulcer
,
pain
,
chronic pain
,
lymphedema
,
rheumatoid arthritis
,
spontaneous remission
,
covid-19
Lornoxicam
leukemia
,
b-cell chronic lymphocytic leukemia
,
lymphoid leukemia
,
neoplasms
,
large b-cell lymphoma diffuse
,
b-cell lymphoma
,
breast neoplasms
,
colorectal neoplasms
,
neoplasm metastasis
,
sarcoma
,
rhabdomyosarcoma
,
neuroblastoma
,
medulloblastoma
,
t-cell lymphoma
,
t-cell lymphoma peripheral
,
myelodysplastic syndromes
,
myeloproliferative disorders
,
multiple myeloma
,
hematologic diseases
,
anemia
,
hodgkin disease
,
aplastic anemia
,
preleukemia
,
myeloid leukemia chronic-phase
,
b-cell leukemia
,
lymphoma
,
non-hodgkin lymphoma
VOLIXIBAT
overweight
,
healthy volunteers/patients
,
non-alcoholic fatty liver disease
,
fatty liver
,
alcoholic fatty liver
,
cholestasis
,
pruritus
,
pregnancy complications
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
,
digestive system diseases
,
cholangitis
Aspartame
post-traumatic stress disorders
,
traumatic stress disorders acute
SHP626
overweight
,
healthy volunteers/patients
,
non-alcoholic fatty liver disease
,
fatty liver
,
alcoholic fatty liver
,
cholestasis
,
pruritus
,
pregnancy complications
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
,
digestive system diseases
,
cholangitis
Histone-arginine methyltransferase carm1
pharmacokinetics
,
chronic obstructive pulmonary disease
,
respiratory aspiration
,
positron-emission tomography
,
anemia
,
alzheimer disease
,
diagnostic imaging
,
medical sociology
,
drug interactions
,
electrocardiography
,
therapeutic equivalency
,
neuroinflammatory diseases
,
pharmacological phenomena
,
dietary fats
,
liver diseases
,
stomach neoplasms
,
hypophosphatemia
,
hematologic neoplasms
,
cystic fibrosis
,
pseudomonas infections
,
biological availability
,
castration-resistant prostatic neoplasms
,
heart failure
,
non-small-cell lung carcinoma
,
breast neoplasms
,
postcoital contraception
,
ovulation inhibition
,
atrial fibrillation
,
lung neoplasms
,
sclerosis
,
parkinson disease
,
small cell lung carcinoma
,
ovarian neoplasms
,
ovarian epithelial carcinoma
,
eczema
,
multiple myeloma
,
plasma cell neoplasms
,
tinnitus
,
leukemia
,
bcr-abl positive chronic myelogenous leukemia
,
myeloid leukemia
,
heart diseases
,
cardiomyopathies
,
libido
,
leiomyoma
,
myofibroma
,
overactive urinary bladder
,
hormonal contraception
,
unplanned pregnancy
,
b-cell lymphoma
,
erythema
,
skin abnormalities
,
myocardial infarction
,
hiv infections
,
acquired immunodeficiency syndrome
,
magnetic resonance angiography
,
tinea pedis
,
left ventricular dysfunction
,
ventricular dysfunction
,
coronary disease
,
myocardial ischemia
,
interstitial lung diseases
,
thyroid neoplasms
,
thyroid diseases
,
pancreatic neoplasms
,
varicose ulcer
,
ulcer
,
leg ulcer
,
dialysis
,
prostatic hyperplasia
,
hyperplasia
,
angina pectoris
,
stable angina
,
ischemic stroke
,
stroke
,
cerebral infarction
,
urologic neoplasms
,
head and neck neoplasms
,
thromboembolism
,
venous thromboembolism
,
pulmonary hypertension
,
hyperphosphatemia
,
chronic renal insufficiency
,
multiple sclerosis
,
non-hodgkin lymphoma
,
lymphoma
,
prostatic neoplasms
,
surgical blood loss
,
venous thrombosis
,
acne vulgaris
,
essential hypertension
,
kidney diseases
,
thrombosis
,
lung diseases
,
hemorrhage
,
endometriosis
,
peripheral vascular diseases
,
postoperative hemorrhage
,
pulmonary embolism
,
cardiovascular diseases
,
hemophilia b
,
spinal cord injuries
,
peripheral arterial disease
,
renal artery obstruction
,
pain
,
bacterial infections
,
low back pain
,
back pain
,
syndrome
,
intraabdominal infections
,
chagas disease
,
chronic progressive multiple sclerosis
,
blood coagulation disorders
,
hormone replacement therapy
,
hyperlipidemias
,
hyperlipoproteinemias
,
choroidal neovascularization
,
myopia
,
degenerative myopia
,
pathologic neovascularization
,
metrorrhagia
,
aspiration pneumonia
,
lung abscess
,
pelvic pain
,
pelvic infection
,
pelvic inflammatory disease
,
dysmenorrhea
,
metabolic bone diseases
,
premenstrual dysphoric disorder
,
diabetic nephropathies
,
proteinuria
,
follicular lymphoma
,
wounds and injuries
,
brain neoplasms
,
cardiovascular abnormalities
,
pathologic constriction
,
onychomycosis
,
vascular diseases
,
memory disorders
,
carotid stenosis
,
pulmonary arterial hypertension
,
burns
,
depression
,
depressive disorder
,
aortic valve stenosis
,
heart valve diseases
,
ventricular outflow obstruction
,
abscess
,
abdominal abscess
,
erectile dysfunction
,
contraception
,
neoplasms
,
hypertension
,
carcinoma
,
hemophilia a
,
healthy volunteers/patients
,
renal cell carcinoma
,
common cold
,
infections
,
atopic dermatitis
,
liver neoplasms
,
pneumonia
,
pharyngitis
,
communicable diseases
,
relapsing-remitting multiple sclerosis
,
hot flashes
,
dermatitis
,
hepatocellular carcinoma
,
urinary tract infections
,
diabetes mellitus
,
coronary artery disease
,
headache
,
type 2 diabetes mellitus
,
colorectal neoplasms
,
menorrhagia
,
postmenopause
,
hypogonadism
,
physiological sexual dysfunction
,
magnetic resonance imaging
,
neoplasm metastasis
,
acute coronary syndrome
,
tension-type headache
,
tonsillitis
,
ischemia
,
peripheral nervous system diseases
,
renal insufficiency
,
chronic bronchitis
,
bronchitis
,
acute disease
,
obesity
,
recurrence
,
respiratory tract infections
,
fever
,
ischemic optic neuropathy
,
optic nerve diseases
,
macular edema
,
edema
,
macular degeneration
,
energy metabolism
,
sinusitis
,
maxillary sinusitis
,
community-acquired pneumonia
,
allergic rhinitis
,
rhinitis
,
allergic rhinitis seasonal
,
medicated intrauterine devices
,
wound healing
,
gene expression
,
cell proliferation
,
constipation
,
fibrosis
,
central nervous system neoplasms
,
photoallergic dermatitis
,
phototoxic dermatitis
,
four-dimensional computed tomography
Surlorian
healthy volunteers/patients
,
allergic rhinitis
,
rhinitis
,
allergic rhinitis seasonal
,
gastrointestinal diseases
,
intestinal diseases
,
ileus
,
dry eye syndromes
,
opioid-induced constipation
,
constipation
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