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Mirum Pharmaceuticals
Mirum Pharmaceuticals
(MIRM)
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Clinical Trials
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Revenue by Drug
Marketed Drugs
Therapeutic Areas:
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Classification:
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Include Generics:
Trade Name
Drug Name
Approved
Patent Expires
Indication
Livmarli
Maralixibat
2021-09-29
2031-2040
Pruritus
,
Alagille syndrome
Cholbam
Cholic acid
2015-03-17
Zellweger syndrome
,
Inborn errors metabolism
Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Cholic acid
biliary liver cirrhosis
,
peroxisomal disorders
,
zellweger syndrome
,
inborn errors steroid metabolism
,
cholestasis
,
infantile refsum disease
,
adrenoleukodystrophy
,
refsum disease
Chenodiol
healthy volunteers/patients
,
liver diseases
,
hepatic insufficiency
,
echolocation
,
hyperlipidemias
,
hyperlipoproteinemia type iv
,
metabolic syndrome
,
hypertriglyceridemia
,
familial combined hyperlipidemia
,
syndrome
,
muscle spasticity
,
hereditary spastic paraplegia
,
paraplegia
,
liver cirrhosis
,
irritable bowel syndrome
,
constipation
,
covid-19
,
inborn genetic diseases
,
duchenne muscular dystrophy
,
muscular diseases
,
nervous system diseases
,
x-linked genetic diseases
,
muscular dystrophies
,
neuromuscular diseases
,
atrophic muscular disorders
,
cerebrotendinous xanthomatosis
,
xanthomatosis
,
biliary liver cirrhosis
,
fibrosis
,
obesity
,
malabsorption syndromes
,
morbid obesity
,
diarrhea
,
gallstones
,
cholelithiasis
,
cholecystolithiasis
,
dermatitis
,
type 2 diabetes mellitus
,
peroxisomal disorders
,
zellweger syndrome
,
infantile refsum disease
,
adrenoleukodystrophy
,
refsum disease
Maralixibat
overweight
,
healthy volunteers/patients
,
syndrome
,
biliary liver cirrhosis
,
substance withdrawal syndrome
,
biliary tract diseases
,
bile duct diseases
,
biliary atresia
,
digestive system diseases
,
sclerosing cholangitis
,
alagille syndrome
,
liver diseases
,
intrahepatic cholestasis
,
cholestasis
,
pruritus
Maralixibat chloride
overweight
,
healthy volunteers/patients
,
syndrome
,
biliary liver cirrhosis
,
biliary tract diseases
,
bile duct diseases
,
substance withdrawal syndrome
,
digestive system diseases
,
biliary atresia
,
sclerosing cholangitis
,
alagille syndrome
,
liver diseases
,
intrahepatic cholestasis
,
cholestasis
,
pruritus
Benzocaine
osteoarthritis
,
neoplasms
,
chronic obstructive pulmonary disease
,
arthritis
,
lung diseases
,
obstructive lung diseases
,
psoriatic arthritis
,
allergic rhinitis
,
rhinitis
,
respiratory tract diseases
,
asthma
,
bronchial diseases
,
hemangioma
,
kaposi sarcoma
,
kasabach-merritt syndrome
,
hemangioendothelioma
,
down syndrome
,
syndrome
,
cognitive dysfunction
,
hiv-1
,
pruritus
,
chronic urticaria
,
urticaria
,
breast neoplasms
,
dwarfism
,
crohn disease
,
alopecia areata
,
alopecia
,
candidemia
,
invasive candidiasis
,
renal insufficiency
,
carotid artery diseases
,
atherosclerosis
,
neoplasm metastasis
,
endocrine system diseases
,
laron syndrome
,
pituitary dwarfism
,
juvenile arthritis
,
chronic disease
,
failure to thrive
,
psychotic disorders
,
mood disorders
,
mental disorders
,
hair diseases
,
tobacco use disorder
,
anxiety disorders
,
emphysema
,
pulmonary emphysema
,
ulcerative colitis
,
colitis
,
ulcer
,
pain
,
chronic pain
,
lymphedema
,
rheumatoid arthritis
,
spontaneous remission
,
covid-19
Lornoxicam
b-cell lymphoma
,
inflammatory breast neoplasms
,
immunoglobulin light-chain amyloidosis
,
myeloproliferative disorders
,
primary myelofibrosis
,
promyelocytic leukemia acute
,
myelomonocytic leukemia chronic
,
myelomonocytic leukemia acute
,
myelomonocytic leukemia juvenile
,
acute disease
,
systemic scleroderma
,
diffuse scleroderma
,
sclerosis
,
large b-cell lymphoma diffuse
,
leukemia
,
myeloid leukemia acute
,
precursor cell lymphoblastic leukemia-lymphoma
,
non-hodgkin lymphoma
,
lymphoid leukemia
,
lymphoma
,
myeloid leukemia
,
myelodysplastic syndromes
,
multiple myeloma
,
plasma cell neoplasms
,
bcr-abl positive chronic myelogenous leukemia
,
preleukemia
,
neoplasms
,
b-cell chronic lymphocytic leukemia
,
triple negative breast neoplasms
,
refractory anemia with excess of blasts
,
renal insufficiency
,
hematologic diseases
,
blood protein disorders
,
neoplasms by histologic type
,
paraproteinemias
,
hodgkin disease
,
diabetes mellitus
,
type 1 diabetes mellitus
,
prolymphocytic leukemia t-cell
,
prolymphocytic leukemia
,
recurrence
,
burkitt lymphoma
,
graft vs host disease
,
bronchiolitis obliterans syndrome
,
aplastic anemia
,
breast neoplasms
,
brain stem neoplasms
,
glycogen storage disease type ii
,
glycogen storage disease type iii
,
ovarian neoplasms
,
hematologic neoplasms
VOLIXIBAT
overweight
,
healthy volunteers/patients
,
non-alcoholic fatty liver disease
,
fatty liver
,
alcoholic fatty liver
,
cholestasis
,
pruritus
,
pregnancy complications
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
,
digestive system diseases
,
cholangitis
Aspartame
syndrome
,
dyssomnias
,
smith-magenis syndrome
,
parasomnias
,
circadian rhythm
SHP626
overweight
,
healthy volunteers/patients
,
non-alcoholic fatty liver disease
,
fatty liver
,
alcoholic fatty liver
,
cholestasis
,
pruritus
,
pregnancy complications
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
,
digestive system diseases
,
cholangitis
Histone-arginine methyltransferase carm1
lymphedema
,
ventral hernia
,
hernia
Surlorian
pharmacokinetics
,
chronic obstructive pulmonary disease
,
respiratory aspiration
,
positron-emission tomography
,
anemia
,
alzheimer disease
,
diagnostic imaging
,
sclerosis
,
small cell lung carcinoma
,
medical sociology
,
renal insufficiency
,
drug interactions
,
electrocardiography
,
therapeutic equivalency
,
neuroinflammatory diseases
,
pharmacological phenomena
,
dietary fats
,
liver diseases
,
stomach neoplasms
,
hematologic neoplasms
,
pain
,
biological availability
,
heart failure
,
non-small-cell lung carcinoma
,
postcoital contraception
,
ovulation inhibition
,
breast neoplasms
,
lung neoplasms
,
atrial fibrillation
,
multiple myeloma
,
plasma cell neoplasms
,
tinnitus
,
heart diseases
,
cardiomyopathies
,
cardiovascular diseases
,
parkinson disease
,
libido
,
leiomyoma
,
myofibroma
,
hormonal contraception
,
unplanned pregnancy
,
b-cell lymphoma
,
ovarian neoplasms
,
peripheral nervous system diseases
,
ovarian epithelial carcinoma
,
erythema
,
skin abnormalities
,
myocardial infarction
,
hiv infections
,
acquired immunodeficiency syndrome
,
peripheral arterial disease
,
magnetic resonance angiography
,
tinea pedis
,
pulmonary hypertension
,
left ventricular dysfunction
,
ventricular dysfunction
,
varicose ulcer
,
ulcer
,
leg ulcer
,
prostatic hyperplasia
,
hyperplasia
,
angina pectoris
,
stable angina
,
ischemic stroke
,
stroke
,
ischemia
,
cerebral infarction
,
urologic neoplasms
,
head and neck neoplasms
,
venous thromboembolism
,
thromboembolism
,
chronic renal insufficiency
,
surgical blood loss
,
non-hodgkin lymphoma
,
lymphoma
,
acne vulgaris
,
venous thrombosis
,
multiple sclerosis
,
hyperphosphatemia
,
hemorrhage
,
prostatic neoplasms
,
postoperative hemorrhage
,
thrombosis
,
pulmonary embolism
,
lung diseases
,
hemophilia b
,
essential hypertension
,
endometriosis
,
kidney diseases
,
peripheral vascular diseases
,
bacterial infections
,
low back pain
,
back pain
,
syndrome
,
intraabdominal infections
,
chagas disease
,
chronic progressive multiple sclerosis
,
blood coagulation disorders
,
hormone replacement therapy
,
hyperlipidemias
,
hyperlipoproteinemias
,
choroidal neovascularization
,
myopia
,
degenerative myopia
,
pathologic neovascularization
,
metrorrhagia
,
aspiration pneumonia
,
lung abscess
,
pelvic pain
,
pelvic infection
,
pelvic inflammatory disease
,
dysmenorrhea
,
metabolic bone diseases
,
premenstrual dysphoric disorder
,
diabetic nephropathies
,
proteinuria
,
follicular lymphoma
,
magnetic resonance imaging
,
brain neoplasms
,
onychomycosis
,
memory disorders
,
burns
,
depression
,
depressive disorder
,
spinal cord injuries
,
abscess
,
abdominal abscess
,
erectile dysfunction
,
contraception
,
hypertension
,
neoplasms
,
hemophilia a
,
healthy volunteers/patients
,
common cold
,
infections
,
pneumonia
,
pharyngitis
,
communicable diseases
,
hot flashes
,
diabetes mellitus
,
headache
,
type 2 diabetes mellitus
,
relapsing-remitting multiple sclerosis
,
menorrhagia
,
atopic dermatitis
,
renal cell carcinoma
,
carcinoma
,
acute coronary syndrome
,
coronary artery disease
,
tension-type headache
,
tonsillitis
,
chronic bronchitis
,
bronchitis
,
acute disease
,
postmenopause
,
dermatitis
,
hypogonadism
,
physiological sexual dysfunction
,
colorectal neoplasms
,
urinary tract infections
,
obesity
,
recurrence
,
respiratory tract infections
,
fever
,
macular degeneration
,
energy metabolism
,
community-acquired pneumonia
,
allergic rhinitis
,
rhinitis
,
allergic rhinitis seasonal
,
wound healing
,
gene expression
,
cell proliferation
,
constipation
,
neoplasm metastasis
,
central nervous system neoplasms
Isoxaflutole
healthy volunteers/patients
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