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Mirum Pharmaceuticals
Mirum Pharmaceuticals
(MIRM)
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Therapeutic Areas:
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Classification:
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Include Generics:
Trade Name
Drug Name
Approved
Patent Expires
Indication
Livmarli
Maralixibat
2021-09-29
2031-2040
Pruritus
,
Alagille syndrome
Cholbam
Cholic acid
2015-03-17
Zellweger syndrome
,
Inborn errors metabolism
Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Cholic acid
neurofibromatosis 1
,
neurofibroma
,
hyperlipidemias
,
central nervous system neoplasms
,
neurofibromatoses
,
aging
,
clostridium infections
,
colonic neoplasms
,
rectal neoplasms
,
echolocation
,
hyperlipoproteinemia type iv
,
metabolic syndrome
,
hypertriglyceridemia
,
familial combined hyperlipidemia
,
liver function tests
,
gastric bypass
,
alcoholic hepatitis
,
parkinson disease
,
huntington disease
,
cardiovascular diseases
,
heart diseases
,
hepatitis a
,
alcoholic fatty liver
,
lipoma
,
gastrointestinal diseases
,
digestive system diseases
,
liver neoplasms
,
lipodystrophy
,
rheumatoid arthritis
,
arthritis
,
biliary tract diseases
,
barrett esophagus
,
heart failure
,
cystic fibrosis
,
covid-19
,
muscle spasticity
,
hereditary spastic paraplegia
,
paraplegia
,
irritable bowel syndrome
,
constipation
,
cardiomyopathies
,
disease progression
,
amyloidosis
,
neoplasm metastasis
,
radiation injuries
,
body weight
,
insulin resistance
,
amyotrophic lateral sclerosis
,
motor neuron disease
,
sclerosis
,
cleft palate
,
hypospadias
,
x-linked genetic diseases
,
smith-lemli-opitz syndrome
,
hypertelorism
,
hiv
,
pruritus
,
bile duct diseases
,
adolescent development
,
sarcoidosis
,
polycystic kidney diseases
,
autosomal dominant polycystic kidney
,
cysts
,
obstructive jaundice
,
jaundice
,
esophageal neoplasms
,
head and neck neoplasms
,
end stage liver disease
,
hepatitis d
,
coinfection
,
breast neoplasms
,
cholestasis
,
healthy volunteers/patients
,
intrahepatic cholestasis
,
colorectal neoplasms
,
cerebrotendinous xanthomatosis
,
xanthomatosis
,
malnutrition
,
pregnancy complications
,
glucose intolerance
,
sclerosing cholangitis
,
peroxisomal disorders
,
zellweger syndrome
,
infantile refsum disease
,
adrenoleukodystrophy
,
refsum disease
,
neoplasms
,
adenomatous polyposis coli
,
nasopharyngeal neoplasms
,
adenoma
,
retinal detachment
,
dissociative disorders
,
chronic hepatitis c
,
duodenal neoplasms
,
inborn errors metabolism
,
inborn errors lipid metabolism
,
inborn errors steroid metabolism
,
pregnancy
,
follicular lymphoma
,
inborn genetic diseases
,
sepsis
,
child nutrition disorders
,
ulcerative colitis
,
pouchitis
,
thyroid diseases
,
acute cholecystitis
,
cholecystitis
,
acalculous cholecystitis
,
pancreatitis
,
psoriasis
,
biliary liver cirrhosis
,
liver diseases
,
fibrosis
,
liver cirrhosis
,
non-alcoholic fatty liver disease
,
cholangitis
,
fatty liver
,
type 2 diabetes mellitus
,
diabetes mellitus
,
gallstones
,
cholelithiasis
,
cholecystolithiasis
,
obesity
,
morbid obesity
,
syndrome
,
hepatitis
,
chemical and drug induced liver injury
,
dyspepsia
,
gestational diabetes
,
overweight
,
autoimmune hepatitis
,
fatigue
,
adiposity
,
neonatal hyperbilirubinemia
,
malabsorption syndromes
,
lipid metabolism disorders
,
diarrhea
,
hemolysis
,
hemolytic anemia
,
chronic kidney failure
,
kidney diseases
,
short bowel syndrome
,
cardiac surgical procedures
,
precursor cell lymphoblastic leukemia-lymphoma
,
lymphoid leukemia
,
fontan procedure
,
infections
,
communicable diseases
,
dermatitis
,
brain neoplasms
,
sarcoma
,
germ cell and embryonal neoplasms
,
medulloblastoma
,
retinoblastoma
,
rhabdoid tumor
,
ewing sarcoma
,
rhabdomyosarcoma
,
primitive neuroectodermal tumors
,
hepatoblastoma
,
retinal neoplasms
,
neuroectodermal tumors
,
phenylketonurias
,
appetite regulation
,
ischemia
,
liver transplantation
,
reperfusion injury
,
gastroesophageal reflux
,
metabolism
,
biliary atresia
,
liver regeneration
,
hepatocellular carcinoma
,
cholangiocarcinoma
,
liver failure
,
hyperbilirubinemia
,
hepatomegaly
,
glucosephosphate dehydrogenase deficiency
,
hepatic encephalopathy
,
transjugular intrahepatic portasystemic shunt
,
hepatitis b
,
hepatitis e
Chenodiol
healthy volunteers/patients
,
liver diseases
,
hepatic insufficiency
,
echolocation
,
hyperlipidemias
,
hyperlipoproteinemia type iv
,
metabolic syndrome
,
hypertriglyceridemia
,
familial combined hyperlipidemia
,
syndrome
,
muscle spasticity
,
hereditary spastic paraplegia
,
paraplegia
,
liver cirrhosis
,
irritable bowel syndrome
,
constipation
,
covid-19
,
inborn genetic diseases
,
duchenne muscular dystrophy
,
muscular diseases
,
nervous system diseases
,
x-linked genetic diseases
,
muscular dystrophies
,
neuromuscular diseases
,
atrophic muscular disorders
,
cerebrotendinous xanthomatosis
,
xanthomatosis
,
biliary liver cirrhosis
,
fibrosis
,
obesity
,
malabsorption syndromes
,
morbid obesity
,
gallstones
,
cholelithiasis
,
cholecystolithiasis
,
diarrhea
,
dermatitis
,
type 2 diabetes mellitus
,
peroxisomal disorders
,
zellweger syndrome
,
infantile refsum disease
,
adrenoleukodystrophy
,
refsum disease
Maralixibat
overweight
,
healthy volunteers/patients
,
syndrome
,
biliary liver cirrhosis
,
substance withdrawal syndrome
,
digestive system diseases
,
biliary tract diseases
,
bile duct diseases
,
intrahepatic cholestasis
,
biliary atresia
,
sclerosing cholangitis
,
alagille syndrome
,
cholestasis
,
liver diseases
,
pruritus
Maralixibat chloride
overweight
,
healthy volunteers/patients
,
syndrome
,
biliary liver cirrhosis
,
substance withdrawal syndrome
,
digestive system diseases
,
biliary tract diseases
,
bile duct diseases
,
intrahepatic cholestasis
,
biliary atresia
,
sclerosing cholangitis
,
alagille syndrome
,
liver diseases
,
cholestasis
,
pruritus
Benzocaine
neuroendocrine tumors
,
biliary tract neoplasms
,
carcinoid tumor
,
malignant carcinoid syndrome
,
serotonin syndrome
Lornoxicam
aggression
,
multiple sclerosis
,
myeloid leukemia acute
,
large b-cell lymphoma diffuse
,
osteosarcoma
,
benign fibrous histiocytoma
,
histiocytoma
,
malignant fibrous histiocytoma
,
reactive arthritis
,
brain neoplasms
,
medulloblastoma
,
primitive neuroectodermal tumors
,
infratentorial neoplasms
,
ovarian neoplasms
,
neoplasms
,
fallopian tube neoplasms
,
peritoneal neoplasms
,
sarcoma
,
neuroblastoma
,
ewing sarcoma
,
breast neoplasms
,
lymphoma
,
b-cell lymphoma
,
non-hodgkin lymphoma
,
b-cell chronic lymphocytic leukemia
,
leukemia
,
lymphoid leukemia
,
follicular lymphoma
,
lupus nephritis
,
systemic lupus erythematosus
,
triple negative breast neoplasms
,
thrombocytopenic purpura idiopathic
,
thrombocytopenic purpura
,
purpura
,
nephritis
,
hemophilia a
,
vasculitis
,
granulomatosis with polyangiitis
,
microscopic polyangiitis
,
systemic vasculitis
VOLIXIBAT
overweight
,
healthy volunteers/patients
,
non-alcoholic fatty liver disease
,
fatty liver
,
alcoholic fatty liver
,
cholestasis
,
pruritus
,
pregnancy complications
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
,
digestive system diseases
,
cholangitis
Aspartame
healthy volunteers/patients
,
covid-19
,
obesity
,
adiposity
,
stroke
,
muscle spasticity
,
shoulder pain
SHP626
overweight
,
healthy volunteers/patients
,
non-alcoholic fatty liver disease
,
fatty liver
,
alcoholic fatty liver
,
cholestasis
,
pruritus
,
pregnancy complications
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
,
digestive system diseases
,
cholangitis
Histone-arginine methyltransferase carm1
myeloid leukemia acute
,
healthy volunteers/patients
,
myelodysplastic syndromes
,
renal cell carcinoma
,
streptococcal infections
,
chronic obstructive pulmonary disease
,
respiratory aspiration
,
rectal neoplasms
,
neoplasm metastasis
,
myeloid leukemia
,
b-cell chronic lymphocytic leukemia
,
lymphoid leukemia
,
lung diseases
,
stomach neoplasms
,
esophageal neoplasms
,
glioblastoma
,
small cell lung carcinoma
,
neuroendocrine carcinoma
,
non-small-cell lung carcinoma
,
colorectal neoplasms
,
pancreatic ductal carcinoma
,
prostatic neoplasms
,
lung neoplasms
,
pancreatic neoplasms
,
leukemia
,
triple negative breast neoplasms
,
multiple myeloma
,
colonic neoplasms
,
sarcoma
,
sjogren's syndrome
,
lymphoma
,
amyotrophic lateral sclerosis
,
ovarian neoplasms
,
psychology rejection
,
iron overload
,
astrocytoma
,
oligodendroglioma
,
chronic hepatitis c
,
hepatitis
,
chronic hepatitis
,
hepatitis a
,
malaria
,
sarcopenia
,
idiopathic pulmonary fibrosis
,
pulmonary fibrosis
,
uveitis
,
meningococcal infections
,
osteoarthritis
,
thrombocytopenia
,
hepatocellular carcinoma
,
liver neoplasms
,
obesity
,
heart failure
,
neoplasm micrometastasis
,
uterine cervical neoplasms
,
motor neuron disease
,
hemolytic anemia autoimmune
,
castration-resistant prostatic neoplasms
,
x-linked bulbo-spinal atrophy
,
cardiovascular diseases
,
hyperlipidemias
,
dyslipidemias
,
atherosclerosis
,
vitiligo
,
breast neoplasms
,
arthritis
,
melanoma
,
neoplasms
,
chronic urticaria
,
haemophilus infections
,
liver transplantation
,
diphtheria
,
thrombocytopenic purpura idiopathic
,
covid-19
,
chronic renal insufficiency
,
kidney diseases
,
psoriatic arthritis
,
carcinoma
,
urticaria
,
primary myelofibrosis
,
syndrome
,
tetanus
,
hematologic neoplasms
,
influenza in birds
,
chronic disease
,
gouty arthritis
,
macular edema
,
skin neoplasms
,
osteitis deformans
,
autoimmune hepatitis
,
juvenile arthritis
,
hepatitis b
,
whooping cough
,
haemophilus influenzae
,
hyperphosphatemia
,
chronic hepatitis b
,
patient compliance
,
eosinophilia
,
cryopyrin-associated periodic syndromes
,
cellulitis
,
lupus nephritis
,
systemic lupus erythematosus
,
nephritis
,
retinal diseases
,
vascular diseases
,
eye diseases
,
scotoma
,
polypoidal choroidal vasculopathy
,
h5n1 subtype influenza a virus
,
disease
,
lymphoproliferative disorders
,
neoplasms by histologic type
,
neoplasms by site
,
human influenza
,
kidney transplantation
,
infections
,
hepatitis c
,
fibrosis
,
tick-borne encephalitis
,
encephalitis
,
communicable diseases
,
cystic fibrosis
,
h1n1 subtype influenza a virus
,
hereditary sensory and autonomic neuropathies
,
cytomegalovirus infections
,
rabies
Surlorian
healthy volunteers/patients
,
myeloid leukemia acute
,
myelodysplastic syndromes
,
chronic obstructive pulmonary disease
,
respiratory aspiration
,
congenital abnormalities
,
chromosome aberrations
,
colonic neoplasms
,
rectal neoplasms
,
neoplasm metastasis
,
myeloid leukemia
,
b-cell chronic lymphocytic leukemia
,
lymphoid leukemia
,
lung diseases
,
renal cell carcinoma
,
non-small-cell lung carcinoma
,
colorectal neoplasms
,
leukemia
,
multiple myeloma
,
lung neoplasms
,
pancreatic neoplasms
,
sjogren's syndrome
,
lymphoma
,
amyotrophic lateral sclerosis
,
prostatic neoplasms
,
psychology rejection
,
ovarian neoplasms
,
thrombocytopenia
,
astrocytoma
,
oligodendroglioma
,
sarcoma
,
hepatocellular carcinoma
,
liver neoplasms
,
chronic hepatitis c
,
hepatitis
,
chronic hepatitis
,
hepatitis a
,
pancreatic ductal carcinoma
,
malaria
,
sarcopenia
,
triple negative breast neoplasms
,
gastrointestinal neoplasms
,
gastrointestinal stromal tumors
,
idiopathic pulmonary fibrosis
,
pulmonary fibrosis
,
neoplasm micrometastasis
,
uterine cervical neoplasms
,
uveitis
,
meningococcal infections
,
osteoarthritis
,
obesity
,
heart failure
,
motor neuron disease
,
hemolytic anemia autoimmune
,
castration-resistant prostatic neoplasms
,
x-linked bulbo-spinal atrophy
,
cardiovascular diseases
,
hyperlipidemias
,
dyslipidemias
,
atherosclerosis
,
vitiligo
,
human influenza
,
breast neoplasms
,
arthritis
,
chronic urticaria
,
melanoma
,
haemophilus infections
,
liver transplantation
,
infections
,
thrombocytopenic purpura idiopathic
,
neoplasms
,
covid-19
,
chronic renal insufficiency
,
kidney diseases
,
carcinoma
,
psoriatic arthritis
,
urticaria
,
primary myelofibrosis
,
syndrome
,
influenza in birds
,
diphtheria
,
hematologic neoplasms
,
gouty arthritis
,
macular edema
,
skin neoplasms
,
osteitis deformans
,
autoimmune hepatitis
,
juvenile arthritis
,
h5n1 subtype influenza a virus
,
disease
,
hyperphosphatemia
,
tetanus
,
communicable diseases
,
chronic hepatitis b
,
patient compliance
,
chronic disease
,
eosinophilia
,
cryopyrin-associated periodic syndromes
,
cellulitis
,
lupus nephritis
,
systemic lupus erythematosus
,
nephritis
,
lymphoproliferative disorders
,
neoplasms by histologic type
,
neoplasms by site
,
kidney transplantation
,
hepatitis c
,
fibrosis
,
tick-borne encephalitis
,
encephalitis
,
cystic fibrosis
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