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Mirum Pharmaceuticals
Mirum Pharmaceuticals
(MIRM)
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Clinical Trials
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Revenue by Drug
Marketed Drugs
Therapeutic Areas:
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Classification:
All
Include Generics:
Trade Name
Drug Name
Approved
Patent Expires
Indication
Livmarli
Maralixibat
2021-09-29
2031-2040
Pruritus
,
Alagille syndrome
Cholbam
Cholic acid
2015-03-17
Zellweger syndrome
,
Inborn errors metabolism
Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Cholic acid
inborn errors steroid metabolism
,
cholestasis
,
peroxisomal disorders
,
zellweger syndrome
,
infantile refsum disease
,
adrenoleukodystrophy
,
refsum disease
Chenodiol
healthy volunteers/patients
,
hepatic insufficiency
,
echolocation
,
hyperlipidemias
,
hyperlipoproteinemia type iv
,
metabolic syndrome
,
hypertriglyceridemia
,
familial combined hyperlipidemia
,
syndrome
,
liver diseases
,
cholangitis
,
lipodystrophy
,
familial partial lipodystrophy
,
muscle spasticity
,
hereditary spastic paraplegia
,
paraplegia
,
irritable bowel syndrome
,
constipation
,
biliary atresia
,
biliary liver cirrhosis
,
cerebrotendinous xanthomatosis
,
xanthomatosis
,
liver cirrhosis
,
fibrosis
,
non-alcoholic fatty liver disease
,
fatty liver
,
obesity
,
malabsorption syndromes
,
morbid obesity
,
gallstones
,
cholelithiasis
,
cholecystolithiasis
,
diarrhea
,
dermatitis
,
type 2 diabetes mellitus
,
peroxisomal disorders
,
zellweger syndrome
,
infantile refsum disease
,
adrenoleukodystrophy
,
refsum disease
Maralixibat
overweight
,
healthy volunteers/patients
,
liver cirrhosis
,
biliary liver cirrhosis
,
substance withdrawal syndrome
,
biliary atresia
,
sclerosing cholangitis
,
cholangitis
,
alagille syndrome
,
cholestasis
,
syndrome
,
liver diseases
,
intrahepatic cholestasis
,
fibrosis
,
pruritus
,
cystic fibrosis
,
constipation
Maralixibat chloride
overweight
,
healthy volunteers/patients
,
liver cirrhosis
,
biliary liver cirrhosis
,
substance withdrawal syndrome
,
biliary atresia
,
sclerosing cholangitis
,
cholangitis
,
alagille syndrome
,
syndrome
,
liver diseases
,
cholestasis
,
intrahepatic cholestasis
,
fibrosis
,
pruritus
,
cystic fibrosis
,
constipation
Benzocaine
type 1 diabetes mellitus
,
type 2 diabetes mellitus
,
hypoglycemia
,
chronic hepatitis
,
liver cirrhosis
,
fibrosis
,
hiv
,
castration-resistant prostatic neoplasms
,
non-small-cell lung carcinoma
,
lung neoplasms
,
alzheimer disease
,
dementia
,
thyroid neoplasms
,
thyroid diseases
,
diabetes mellitus
,
hepatitis c
,
hepatitis
,
chronic hepatitis c
,
hepatitis a
,
hiv infections
,
acquired immunodeficiency syndrome
,
hiv-2
,
immunologic deficiency syndromes
,
small cell lung carcinoma
,
hypertension
,
coronary artery disease
,
myocardial ischemia
,
dyslipidemias
,
atherosclerosis
,
rheumatoid arthritis
,
arthritis
,
neuromuscular blockade
,
prostatic neoplasms
,
anesthesia
,
acute coronary syndrome
,
chronic renal insufficiency
,
kidney diseases
,
leiomyoma
,
endometriosis
,
cholecystitis
,
uterine prolapse
,
intestinal obstruction
,
prolapse
,
spinal diseases
,
delayed emergence from anesthesia
,
laryngoscopy
,
laparoscopy
,
muscle relaxation
,
obesity
,
disease
,
gastric bypass
,
respiration
,
urinary retention
,
infertility
,
female infertility
,
uterine diseases
,
postoperative complications
,
pneumonia
,
wound infection
,
surgical wound infection
Lornoxicam
hematologic diseases
,
lymphoma
,
t-cell lymphoma
,
t-cell lymphoma peripheral
VOLIXIBAT
overweight
,
healthy volunteers/patients
,
non-alcoholic fatty liver disease
,
fatty liver
,
alcoholic fatty liver
,
cholangitis
,
pregnancy complications
,
cholestasis
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
Sodium chloride
duchenne muscular dystrophy
,
muscular dystrophies
Aspartame
lymphoma
,
conjunctivitis
,
allergic rhinitis
,
rhinitis
,
allergic conjunctivitis
,
liver neoplasms
,
atopic dermatitis
,
dermatitis
,
healthy volunteers/patients
,
vomiting
,
nausea
,
infections
,
prostatic neoplasms
,
postoperative nausea and vomiting
,
recurrence
,
brain neoplasms
,
second primary neoplasms
,
depression
,
treatment-resistant depressive disorder
,
depressive disorder
,
esophageal neoplasms
,
esophageal squamous cell carcinoma
,
hematologic neoplasms
,
pneumonia
,
pseudomonas infections
,
pseudomonas aeruginosa
,
bacteremia
,
renal cell carcinoma
,
liver cirrhosis
,
experimental liver cirrhosis
,
chronic obstructive pulmonary disease
,
nasopharyngeal carcinoma
,
nasopharyngeal neoplasms
,
melanoma
,
colorectal neoplasms
,
pancreatic ductal carcinoma
,
gastrointestinal neoplasms
,
biliary tract neoplasms
,
urinary bladder neoplasms
,
non-muscle invasive bladder neoplasms
,
non-small-cell lung carcinoma
,
lung neoplasms
,
hiv infections
,
neoplasms
,
acquired immunodeficiency syndrome
,
breast neoplasms
,
carcinoma
,
ovarian neoplasms
,
triple negative breast neoplasms
,
uterine cervical neoplasms
,
condylomata acuminata
,
fibrosis
,
hepatocellular carcinoma
,
ovarian epithelial carcinoma
,
hiv-2
,
immunologic deficiency syndromes
,
hiv-1
,
antibiotic prophylaxis
,
hepatitis b
,
chronic hepatitis b
,
coronary disease
,
coronary artery disease
,
myocardial ischemia
,
heart diseases
,
lung diseases
,
cystic fibrosis
,
pulmonary hypertension
,
pulmonary arterial hypertension
,
endometrial neoplasms
,
adenocarcinoma
,
fallopian tube neoplasms
,
asthma
,
chronic hepatitis c
,
hepatitis
,
hepatitis a
,
hypertension
,
hepatitis c
,
hiv
,
neuromuscular blockade
,
chronic kidney failure
,
kidney diseases
,
chronic hepatitis
,
intestinal diseases
,
non-hodgkin lymphoma
,
infertility
,
schizophrenia
,
traumatic brain injuries
,
brain concussion
,
brain injuries
,
post-concussion syndrome
,
papillomavirus infections
,
uterine cervical dysplasia
SHP626
overweight
,
healthy volunteers/patients
,
non-alcoholic fatty liver disease
,
fatty liver
,
alcoholic fatty liver
,
cholangitis
,
pregnancy complications
,
cholestasis
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
Arm1
low back pain
,
back pain
Arm2
low back pain
,
back pain
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